Guigliani, RobertoLopez, Antonio Gonzalez-MenesesScarpa, MaurizioLau, HeatherZhang, LinMalkus, BetsyMarsden, DeborahMerritt, J. Lawrence, II2023-05-032023-05-032022-03-211098-3600http://hdl.handle.net/10668/22252enVestronidase alfa for the treatment of Mucopolysaccharidosis VII (MPS VII): Updated results from a novel, longitudinal, multicenter disease monitoring programconference outputopen access10.1016/j.gim.2022.01.2021530-0366http://www.gimjournal.org/article/S1098360022002192/pdf788465500155