RT Conference Proceedings T1 Vestronidase alfa for the treatment of Mucopolysaccharidosis VII (MPS VII): Updated results from a novel, longitudinal, multicenter disease monitoring program A1 Guigliani, Roberto A1 Lopez, Antonio Gonzalez-Meneses A1 Scarpa, Maurizio A1 Lau, Heather A1 Zhang, Lin A1 Malkus, Betsy A1 Marsden, Deborah A1 Merritt, J. Lawrence, II PB Elsevier science inc SN 1098-3600 YR 2022 FD 2022-03-21 LK http://hdl.handle.net/10668/22252 UL http://hdl.handle.net/10668/22252 LA en DS RISalud RD Apr 8, 2025