TY - RPRT AU - Acosta García, Héctor PY - 2018 SN - 978-84-1763-20-4 UR - http://hdl.handle.net/10668/3780 T2 - Síntesis de la evidencia: medicamentos AB - Se evalúa la eficacia y seguridad de velmanasa alfa en el tratamiento de la alfa-manosidosis a través de una revisión rápida que sirve de apoyo para el posicionamiento terapéutico. Velmanasa alfa ha demostrado tener actividad biológica a través de la... LA - spa A3 - Agencia de Evaluación de Tecnologías Sanitarias de Andalucía KW - Alfa-manosidosis KW - Terapia de reemplazo enzimático KW - Síntesis de la evidencia I KW - Quimioterapia KW - Oligosacáridos KW - Resultado del tratamiento KW - Medicina basada en la evidencia KW - Alpha-Mannosidosis KW - Drug therapy KW - Oligosaccharides KW - Treatment outcome KW - Evidence-based medicine KW - Medical Subject Headings::Diseases::Congenital, Hereditary, and Neonatal Diseases and Abnormalities::Genetic Diseases, Inborn::Metabolism, Inborn Errors::Carbohydrate Metabolism, Inborn Errors::Mannosidase Deficiency Diseases::alpha-Mannosidosis KW - Medical Subject Headings::Analytical, Diagnostic and Therapeutic Techniques and Equipment::Therapeutics::Drug Therapy::Enzyme Therapy::Enzyme Replacement Therapy KW - Medical Subject Headings::Analytical, Diagnostic and Therapeutic Techniques and Equipment::Diagnosis::Prognosis::Treatment Outcome KW - Medical Subject Headings::Disciplines and Occupations::Health Occupations::Medicine::Clinical Medicine::Evidence-Based Medicine KW - Medical Subject Headings::Diseases::Congenital, Hereditary, and Neonatal Diseases and Abnormalities::Genetic Diseases, Inborn::Metabolism, Inborn Errors::Lysosomal Storage Diseases::Mannosidase Deficiency Diseases::alpha-Mannosidosis KW - Medical Subject Headings::Analytical, Diagnostic and Therapeutic Techniques and Equipment::Therapeutics::Drug Therapy KW - Medical Subject Headings::Chemicals and Drugs::Carbohydrates::Polysaccharides::Oligosaccharides TI - Velmanasa alfa en el tratamiento de la alfa-manosidosis: eficacia y seguridad TY - report ER -