TY  - JOUR
AU  - Gomez-Pastrana, David
AU  - Nwokoro, Chinedu
AU  - McLean, Mike
AU  - Brown, Sarah
AU  - Christiansen, Nanna
AU  - Pao, Caroline S
PY  - 2018
DO  - 10.1016/j.anpedi.2018.05.022
UR  - http://hdl.handle.net/10668/12817
T2  - Anales de pediatria
AB  - Ivacaftor is a cystic fibrosis transmembrane conductance regulator (CFTR) potentiator that has been shown to improve the nutritional status and lung function of cystic fibrosis patients with the G551D mutation in clinical trials. The objective of this...
LA  - es
KW  - Cystic fibrosis
KW  - Fibrosis quística
KW  - Ivacaftor
KW  - Real-life
KW  - Vida real
KW  - Adolescent
KW  - Aminophenols
KW  - Aspergillosis, Allergic Bronchopulmonary
KW  - Child
KW  - Chloride Channel Agonists
KW  - Cystic Fibrosis
KW  - Cystic Fibrosis Transmembrane Conductance Regulator
KW  - Female
KW  - Genotype
KW  - Humans
KW  - Male
KW  - Mutation
KW  - Mycobacterium Infections, Nontuberculous
KW  - Mycobacterium abscessus
KW  - Nutritional Status
KW  - Pseudomonas Infections
KW  - Pseudomonas aeruginosa
KW  - Quinolones
KW  - Treatment Outcome
TI  - [Real-world effectiveness of ivacaftor in children with cystic fibrosis and the G551D mutation].
T2  - Efectividad de ivacaftor en vida real en niños con fibrosis quística y mutación G551D.
TY  - research article
VL  - 90
ER  -