TY - JOUR AU - Coote, David J AU - Davis, Mark R AU - Cabrera, Macarena AU - Needham, Merrilee AU - Laing, Nigel G AU - Nowak, Kristen J PY - 2018 DO - 10.1038/s41431-017-0013-2 UR - http://hdl.handle.net/10668/12008 T2 - European journal of human genetics : EJHG LA - en KW - Child, Preschool KW - Genetic Counseling KW - Humans KW - Male KW - Muscle, Skeletal KW - Muscular Dystrophy, Duchenne TI - CUGC for Duchenne muscular dystrophy (DMD). TY - research article VL - 26 ER -