TY - JOUR AU - Galan, Lucia AU - Gonzalez-Moreno, Juan AU - Martínez-Sesmero, José Manuel AU - Muñoz-Beamud, Francisco AU - Santos-Rubio, Maria Dolores AU - Tran, Diana AU - Lebeau, Paul AU - Stewart, Michelle AU - Mallaina, Pablo AU - Tarilonte, Patricia AU - Peral, Carmen AU - Rozenbaum, Mark H PY - 2021 DO - 10.1080/14737167.2021.1900738 UR - http://hdl.handle.net/10668/17355 T2 - Expert review of pharmacoeconomics & outcomes research AB - Background: Transthyretin amyloid polyneuropathy (ATTR-PN) is a fatal disease associated with substantial burden of illness. Three therapies are approved by the European Medicines Agency for the management of this rare disease. The aim of this study... LA - en KW - Hereditary amyloidosis KW - onpattro KW - rare disease KW - tegsedi KW - treatment cost analysis KW - vyndaqel KW - Amyloid Neuropathies, Familial KW - Benzoxazoles KW - Cost of Illness KW - Drug Costs KW - Health Care Costs KW - Hospitalization KW - Humans KW - Oligonucleotides KW - RNA, Small Interfering KW - Spain TI - Estimating the annual economic burden for the management of patients with transthyretin amyloid polyneuropathy in Spain. TY - research article VL - 21 ER -