TY  - JOUR
AU  - Jacobs, Marni B
AU  - James, Meredoith K
AU  - Lowes, Linda P
AU  - Alfano, Lindsay N
AU  - Eagle, Michelle
AU  - Muni-Lofra, Robert
AU  - Moore, Ursula
AU  - Feng, Jia
AU  - Rufibach, Laura E
AU  - Rose, Kristy
AU  - Duong, Tina
AU  - Bello, Luca
AU  - Pedrosa-Hernandez, Irene
AU  - Holsten, Scott
AU  - Sakamoto, Chikako
AU  - Canal, Aurelie
AU  - Sanchez-Aguilera-Praxedes, Nieves
AU  - Thiele, Simone
AU  - Siener, Catherine
AU  - Vandevelde, Bruno
AU  - DeWolf, Brittney
AU  - Maron, Elke
AU  - Guglieri, Michela
AU  - Hogrel, Jean-Yves
AU  - Blamire, Andrew M
AU  - Carlier, Pierre G
AU  - Spuler, Simone
AU  - Day, John W
AU  - Jones, Kristi J
AU  - Bharucha-Goebel, Diana X
AU  - Salort-Campana, Emmanuelle
AU  - Pestronk, Alan
AU  - Walter, Maggie C
AU  - Paradas, Carmen
AU  - Stojkovic, Tanya
AU  - Mori-Yoshimura, Madoka
AU  - Bravver, Elena
AU  - Diaz-Manera, Jordi
AU  - Pegoraro, Elena
AU  - Mendell, Jerry R
AU  - Mayhew, Anna G
AU  - Straub, Volker
PY  - 2021
DO  - 10.1002/ana.26044
UR  - http://hdl.handle.net/10668/17164
T2  - Annals of neurology
AB  - Dysferlinopathy is a muscular dystrophy with a highly variable clinical presentation and currently unpredictable progression. This variability and unpredictability presents difficulties for prognostication and clinical trial design. The Jain Clinical...
LA  - en
PB  - John Wiley & Sons, Inc.
KW  - Adolescent
KW  - Aged
KW  - Clinical Trials as Topic
KW  - Female
KW  - Male
KW  - Psychometrics
KW  - Adult
KW  - Age of Onset
KW  - Aged, 80 and over
KW  - Child
KW  - Cohort Studies
KW  - Disease Progression
KW  - Humans
KW  - Longitudinal Studies
KW  - Middle Aged
KW  - Muscular Dystrophies, Limb-Girdle
KW  - Treatment Outcome
KW  - Young Adult
TI  - Assessing Dysferlinopathy Patients Over Three Years With a New Motor Scale.
TY  - research article
VL  - 89
ER  -