TY - JOUR AU - Facey, Karen M AU - Espin, Jaime AU - Kent, Emma AU - Link, Angel AU - Nicod, Elena AU - O'Leary, Aisling AU - Xoxi, Entela AU - van de Vijver, Inneke AU - Zaremba, Anna AU - Benisheva, Tatyana AU - Vagoras, Andrius AU - Upadhyaya, Sheela PY - 2021 DO - 10.1007/s40273-021-01050-5 UR - http://hdl.handle.net/10668/18169 T2 - PharmacoEconomics AB - Enthusiasm for the use of outcomes-based managed entry agreements (OBMEAs) to manage uncertainties apparent at the time of appraisal/pricing and reimbursement of new medicines has waned over the past decade, as challenges in establishment,... LA - en PB - SpringerNature KW - Outcomes-based managed entry agreements (OBMEAs) KW - Rare diseases KW - Reimbursement frameworks KW - Health technology assessment (HTA) KW - Data collection systems KW - Coverage with evidence development (CED) KW - Costs and Cost Analysis KW - Humans KW - Oligonucleotides KW - Rare Diseases KW - Receptors, Antigen, T-Cell KW - Technology Assessment, Biomedical TI - Implementing Outcomes-Based Managed Entry Agreements for Rare Disease Treatments: Nusinersen and Tisagenlecleucel. TY - research article VL - 39 ER -